Title: | Systemic Delivery of scAAV9 expressing SMN prolongs survival in a model of spinal muscular atrophy |
Journal : | Science translational medicine, 2, 35, 35ra42 |
Authors: | Valori CF ; Ning K ; Wyles M ; Mead RJ ; Grierson AJ ; Shaw PJ ; Azzouz M |
Material Type: | Article |
Publication Date: | 9/06/2010 |
Size: | p. 1-8 |
Languages: | English |
Keywords : | AAV9 vectors ; cell cultures ; gene therapy ; immunocytochemistry ; immunohistochemistry ; life expectancy ; mouse model ; SMN genes ; spinal muscular atrophy ; survival rate |
Abstract: |
Accès au résumé PubMed / to PubMed abstract |
Lien associé : | http://www.ncbi.nlm.nih.gov/pubmed/20538619 |
Pubmed / DOI : | DOI : 10.1126/scitranslmed.3000830 |
See also : |