Title: | Rescue of a Dystrophin-like protein by Exon Skipping In Vivo restores GABA(A)-receptor Clustering in the Hippocampus of the mdx Mouse |
Journal : | Molecular therapy, 18, 9 |
Authors: | Vaillend C ; Perronnet C ; Ros C ; Gruszczynski C ; Goyenvalle A ; Laroche S ; Danos O ; Garcia L ; Peltékian E |
Material Type: | Article |
Publication Date: | 2010 |
Size: | p. 1683-1688 |
Languages: | English |
Keywords : | adenoassociated vectors ; brain ; Duchenne muscular dystrophy ; dystrophin ; exon ; exon skipping ; GABA receptors ; gene therapy ; immunohistochemistry ; mdx mouse ; molecular genetics ; RNA ; skeletal muscle |
Abstract: |
Accès au résumé PubMed / to PubMed abstract |
Lien associé : | http://www.ncbi.nlm.nih.gov/pubmed/20588257 |
Pubmed / DOI : | DOI : 10.1038/mt.2010.134 |