Title: | Gene therapy for muscular dystrophy: Lessons learned and path forward |
Journal : | Neuroscience letters, 527, 2 |
Authors: | Mendell JR ; Rodino-Klapac L ; Sahenk Z ; Malik V ; Kaspar BK ; Walker CM ; Clark KR |
Material Type: | Article |
Publication Date: | 2012 |
Size: | p. 90-99 |
Languages: | English |
Keywords : | adenoassociated vectors ; alpha-sarcoglycan ; diagrams ; DYS gene ; dystrophin ; enzymotherapy ; exon skipping ; follistatin ; gene therapy ; gene transfer ; neuromuscular disease ; review article ; therapeutic prospects |
Abstract: |
Accès au résumé PubMed / to PubMed abstract |
Lien associé : | http://www.ncbi.nlm.nih.gov/entrez/query.fcgi?cmd=Retrieve&db=PubMed&dopt=Citation&list_uids=22609847 |
Pubmed / DOI : | DOI : 10.1016/j.neulet.2012.04.078 |