Title: | Sustained expression and safety of human GNE in normal mice after gene transfer based on AAV8 systemic delivery |
Journal : | Neuromuscular disorders : NMD, 22, 11 |
Authors: | Mitrani-Rosenbaum S ; Yakovlev L ; Becker Cohen M ; Telem M ; Elbaz M ; Yanay N ; Yotvat H ; Ben Shlomo U ; Harazi A ; Fellig Y ; Argov Z ; Sela I |
Material Type: | Article |
Publication Date: | 2012 |
Size: | p. 1015-1024 |
Languages: | English |
Keywords : | AAV8 vectors ; animal models ; diagrams ; gene therapy ; gene transfer ; GNE gene ; human ; injection ; mouse |
Abstract: |
Accès au résumé PubMed / to PubMed abstract |
Lien associé : | http://www.ncbi.nlm.nih.gov/entrez/query.fcgi?cmd=Retrieve&db=PubMed&dopt=Citation&list_uids=22633753 |
Pubmed / DOI : | DOI : 10.1016/j.nmd.2012.03.013 |