Title: | Ataluren as an agent for therapeutic nonsense suppression |
Journal : | Annual review of medicine, 64 |
Authors: | Peltz SW ; Morsy M ; Welch EM ; Jacobson A |
Material Type: | Article |
Publication Date: | 2013 |
Size: | p. 407-425 |
Languages: | English |
Keywords : | aminosides ; ataluren ; carnitine palmitoyltransferase 1 ; clinical trials ; cystic fibrosis ; drugs ; Duchenne muscular dystrophy ; Miyoshi distal myopathy ; nonsense mutations ; terminator codons ; translation (genetics) |
Abstract: | Accès au résumé Pubmed/to pubmed abstract |
Pubmed / DOI : | DOI : 10.1146/annurev-med-120611-144851 |