Title: | Dystrophin rescue by trans-splicing : a strategy for DMD genotypes not eligible for exon skipping approaches |
Journal : | Nucleic acids research, 41, 17 |
Authors: | Lorain S ; Peccate C ; Le Hir M ; Griffith G ; Philippi S ; Precigout G ; Mamchaoui K ; Jollet A ; Voit T ; Garcia L |
Material Type: | Article |
Publication Date: | 2013 |
Size: | p. 8391-8402 |
Languages: | English |
Keywords : | adenoassociated vectors ; antisense oligonucleotides ; Duchenne muscular dystrophy ; dystrophin ; exon skipping ; in vitro ; intramuscular injection ; mdx mouse ; messenger RNA ; splicing |
Abstract: |
Accès au résumé PubMed / to PubMed abstract |
Lien associé : | http://www.ncbi.nlm.nih.gov/pubmed/23861443 |
Pubmed / DOI : | DOI : 10.1093/nar/gkt621 |
See also : |