Title: | Autologous myoblast transplantation for oculopharyngeal muscular dystrophy : a phase I/IIa clinical study |
Journal : | Molecular therapy, 22, 1 |
Authors: | Perie S ; Trollet C ; Mouly V ; Vanneaux V ; Mamchaoui K ; Bouazza B ; Pierre Marolleau J ; Laforet P ; Chapon F ; Eymard B ; Butler Browne G ; Larghero J ; Lacau Saint Guily J |
Material Type: | Article |
Publication Date: | 2014 |
Size: | p. 219-225 |
Languages: | English |
Keywords : | autografts ; cell therapy ; dysphagia ; medical treatment ; myoblast ; oculopharyngeal muscular dystrophy ; phase 1/2 clinical trials ; quality of life ; swallowing disorders |
Abstract: |
Accès au résumé PubMed / to PubMed abstract |
Pubmed / DOI : | DOI : 10.1038/mt.2013.155 / Pubmed : 23831596 |
See also : |
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Mol_Ther_2014,_22(1)-p._219-225.pdf Adobe Acrobat PDF |