Title: | Evidence for long-term efficacy and safety of gene therapy for Wiskott-Aldrich syndrome in preclinical models |
Journal : | Current opinion in molecular therapeutics, 17, 6 |
Authors: | Marangoni F ; Bosticardo M ; Charrier S ; Draghici E ; Locci M ; Scaramuzza S ; Panaroni C ; Ponzoni M ; Sanvito F ; Doglioni C ; Liabeuf M ; Gjata B ; Montus M ; Siminovitch K ; Aiuti A ; Naldini L ; Dupré la Tour M ; Roncarolo MG ; Galy A ; Villa A |
Material Type: | Article |
Publication Date: | 2009 |
Size: | p. 1073-1082 |
Languages: | English |
Keywords : | biomedical research |
Pubmed / DOI : | Pubmed : 19259069 |