Title: | Protocol for a phase II, monocentre, double-blind, placebo-controlled, cross-over trial to assess efficacy of pyridostigmine in patients with spinal muscular atrophy types 2-4 (SPACE trial) |
Journal : | BMJ Open, 8, 7 |
Authors: | Stam M, Author ; Stam M ; Wadman RI ; Wijngaarde CA ; Bartels B ; Asselman FL ; Otto LAM ; Goedee HS ; Habets LE ; de Groot JF ; Schoenmakers MAGC ; Cuppen I ; van den Berg LH ; van der Pol WL |
Material Type: | Article |
Publication Date: | 2018 |
Languages: | English |
Keywords: | cross-over;fatigability;neuromuscular junction;pyridostigmine;sma;spinal muscular atrophy; |
Pubmed / DOI : | DOI : 10.1136/bmjopen-2017-019932 / Pubmed : 30061431 |
N° Profil MNM : | 2018073 |
Link for e-copy: | http://www.ncbi.nlm.nih.gov/pubmed/30061431 |