Title: | Aceneuramic Acid Extended Release Administration Maintains Upper Limb Muscle Strength in a 48-week Study of Subjects with GNE Myopathy: Results from a Phase 2, Randomized, Controlled Study |
Journal : | Journal of Neuromuscular Diseases, 3, 1 |
Authors: | Argov Z, Author ; Caraco Y ; Lau H ; Pestronk A ; Shieh PB ; Skrinar A ; Koutsoukos T ; Ahmed R ; Martinisi J ; Kakkis E |
Material Type: | Article |
Publication Date: | 2016 |
Size: | p 49 |
Languages: | English |
Keywords : | dietary supplements ; GNE myopathy ; muscle strength ; phase 2 clinical trials ; sialic acid ; upper limbs |
Keywords: | GNE Myopathy;Sialic acid;distal myopathy with rimmed vacuoles;hereditary inclusion body myopathy;myopathy therapy; |
Pubmed / DOI : | DOI : 10.3233/JND-159900 / Pubmed : 27854209 |
Link for e-copy: | http://www.ncbi.nlm.nih.gov/pubmed/27854209 |
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