Title: | Myology 2016 : 5th International Congress of Myology ; Plenary session - SMA and Therapeutics |
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Authors: | 5th International Congress of Myology (14-18 March 2016; Centre convention, Lyon, France), Issuing body ; Finkel R, Author ; Mendell J, Author ; Biondi O, Author |
Material Type: | Article |
Publisher: | AFM-TELETHON, 17/03/2016 |
Size: | p. 18-19 |
Languages: | English |
Keywords : | antisense oligonucleotides ; CHOP INTEND motor function scale ; clinical trials ; gene therapy ; muscle exercise ; pharmacotherapy ; proximal spinal muscular atrophy type 1 ; proximal spinal muscular atrophy type 2 ; proximal spinal muscular atrophy type 3 ; SMN1 gene ; SMN2 gene ; symposium |
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