Title: | Evaluation of Readministration of a Recombinant Adeno-Associated Virus Vector Expressing Acid Alpha-Glucosidase in Pompe Disease: Preclinical to Clinical Planning. |
Journal : | Human gene therapy. Clinical development, 26, 3 |
Authors: | Corti M ; Cleaver B ; Clément N ; Conlon TJ ; Faris KJ ; Wang G ; Benson J ; Tarantal AF ; Fuller D ; Herzog RW ; Byrne BJ |
Material Type: | Article |
Publication Date: | 2015 |
ISBN (or other code): | 26390092 |
Size: | 185-93 |
Languages: | English |
Keywords : | cross-sectional study ; late-onset Pompe disease |
Pubmed / DOI : | DOI : 10.1089/humc.2015.068 / Pubmed : 26390092 |
Link for e-copy: | http://www.ncbi.nlm.nih.gov/pubmed/26390092 |