Titre : | Quality of life data for individuals affected by spinal muscular atrophy: a baseline dataset from the Cure SMA Community Update Survey |
Revue : | Orphanet journal of rare diseases, 15, 1 |
Auteurs : | Belter L ; Cruz R ; Jarecki J |
Type de document : | Article |
Année de publication : | 2020 |
Pages : | p 217 |
Langues: | Anglais |
Mots-clés: | Health related quality of life;Health utilities index;PROMIS fatigue short form;Patient reported outcome measures;Spinal muscular atrophy;Work productivity and activity impairment; |
Pubmed / DOI : | Pubmed : 32838797 / DOI : 10.1186/s13023-020-01498-2 |
N° Profil MNM : | 2020091 |
En ligne : | http://www.ncbi.nlm.nih.gov/pubmed/32838797 |